List of Tables
Table 1. Global Orphan Diseases Market Size Growth Rate by Therapy Area Type (US$ Million): 2020 VS 2024 VS 2031
Table 2. Key Players of Ocology
Table 3. Key Players of Hematology
Table 4. Key Players of Neurology
Table 5. Key Players of Endocrinology
Table 6. Key Players of Cardiovascular
Table 7. Key Players of Respiratory
Table 8. Key Players of Immunotherapy
Table 9. Global Orphan Diseases Market Size Growth by Application (US$ Million): 2020 VS 2024 VS 2031
Table 10. Global Orphan Diseases Market Size by Region (US$ Million): 2020 VS 2024 VS 2031
Table 11. Global Orphan Diseases Market Size by Region (2020-2025) & (US$ Million)
Table 12. Global Orphan Diseases Market Share by Region (2020-2025)
Table 13. Global Orphan Diseases Forecasted Market Size by Region (2026-2031) & (US$ Million)
Table 14. Global Orphan Diseases Market Share by Region (2026-2031)
Table 15. Orphan Diseases Market Trends
Table 16. Orphan Diseases Market Drivers
Table 17. Orphan Diseases Market Challenges
Table 18. Orphan Diseases Market Restraints
Table 19. Global Orphan Diseases Revenue by Players (2020-2025) & (US$ Million)
Table 20. Global Orphan Diseases Market Share by Players (2020-2025)
Table 21. Global Top Orphan Diseases Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Orphan Diseases as of 2024)
Table 22. Ranking of Global Top Orphan Diseases Companies by Revenue (US$ Million) in 2024
Table 23. Global 5 Largest Players Market Share by Orphan Diseases Revenue (CR5 and HHI) & (2020-2025)
Table 24. Global Key Players of Orphan Diseases, Headquarters and Area Served
Table 25. Global Key Players of Orphan Diseases, Product and Application
Table 26. Global Key Players of Orphan Diseases, Date of Enter into This Industry
Table 27. Mergers & Acquisitions, Expansion Plans
Table 28. Global Orphan Diseases Market Size by Therapy Area Type (2020-2025) & (US$ Million)
Table 29. Global Orphan Diseases Revenue Market Share by Therapy Area Type (2020-2025)
Table 30. Global Orphan Diseases Forecasted Market Size by Therapy Area Type (2026-2031) & (US$ Million)
Table 31. Global Orphan Diseases Revenue Market Share by Therapy Area Type (2026-2031)
Table 32. Global Orphan Diseases Market Size by Application (2020-2025) & (US$ Million)
Table 33. Global Orphan Diseases Revenue Market Share by Application (2020-2025)
Table 34. Global Orphan Diseases Forecasted Market Size by Application (2026-2031) & (US$ Million)
Table 35. Global Orphan Diseases Revenue Market Share by Application (2026-2031)
Table 36. North America Orphan Diseases Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 37. North America Orphan Diseases Market Size by Country (2020-2025) & (US$ Million)
Table 38. North America Orphan Diseases Market Size by Country (2026-2031) & (US$ Million)
Table 39. Europe Orphan Diseases Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 40. Europe Orphan Diseases Market Size by Country (2020-2025) & (US$ Million)
Table 41. Europe Orphan Diseases Market Size by Country (2026-2031) & (US$ Million)
Table 42. Asia-Pacific Orphan Diseases Market Size Growth Rate by Region (US$ Million): 2020 VS 2024 VS 2031
Table 43. Asia-Pacific Orphan Diseases Market Size by Region (2020-2025) & (US$ Million)
Table 44. Asia-Pacific Orphan Diseases Market Size by Region (2026-2031) & (US$ Million)
Table 45. Latin America Orphan Diseases Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 46. Latin America Orphan Diseases Market Size by Country (2020-2025) & (US$ Million)
Table 47. Latin America Orphan Diseases Market Size by Country (2026-2031) & (US$ Million)
Table 48. Middle East & Africa Orphan Diseases Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 49. Middle East & Africa Orphan Diseases Market Size by Country (2020-2025) & (US$ Million)
Table 50. Middle East & Africa Orphan Diseases Market Size by Country (2026-2031) & (US$ Million)
Table 51. Bristol-Myers Squibb Company Details
Table 52. Bristol-Myers Squibb Business Overview
Table 53. Bristol-Myers Squibb Orphan Diseases Product
Table 54. Bristol-Myers Squibb Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 55. Bristol-Myers Squibb Recent Development
Table 56. Novartis Company Details
Table 57. Novartis Business Overview
Table 58. Novartis Orphan Diseases Product
Table 59. Novartis Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 60. Novartis Recent Development
Table 61. Celgene Company Details
Table 62. Celgene Business Overview
Table 63. Celgene Orphan Diseases Product
Table 64. Celgene Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 65. Celgene Recent Development
Table 66. Roche Company Details
Table 67. Roche Business Overview
Table 68. Roche Orphan Diseases Product
Table 69. Roche Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 70. Roche Recent Development
Table 71. Pfizer Company Details
Table 72. Pfizer Business Overview
Table 73. Pfizer Orphan Diseases Product
Table 74. Pfizer Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 75. Pfizer Recent Development
Table 76. Alexion Company Details
Table 77. Alexion Business Overview
Table 78. Alexion Orphan Diseases Product
Table 79. Alexion Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 80. Alexion Recent Development
Table 81. Sanofi Company Details
Table 82. Sanofi Business Overview
Table 83. Sanofi Orphan Diseases Product
Table 84. Sanofi Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 85. Sanofi Recent Development
Table 86. Vertex Pharmaceuticals Company Details
Table 87. Vertex Pharmaceuticals Business Overview
Table 88. Vertex Pharmaceuticals Orphan Diseases Product
Table 89. Vertex Pharmaceuticals Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 90. Vertex Pharmaceuticals Recent Development
Table 91. GlaxoSmithKline Company Details
Table 92. GlaxoSmithKline Business Overview
Table 93. GlaxoSmithKline Orphan Diseases Product
Table 94. GlaxoSmithKline Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 95. GlaxoSmithKline Recent Development
Table 96. Merck Company Details
Table 97. Merck Business Overview
Table 98. Merck Orphan Diseases Product
Table 99. Merck Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 100. Merck Recent Development
Table 101. Abbvie Company Details
Table 102. Abbvie Business Overview
Table 103. Abbvie Orphan Diseases Product
Table 104. Abbvie Revenue in Orphan Diseases Business (2020-2025) & (US$ Million)
Table 105. Abbvie Recent Development
Table 106. Research Programs/Design for This Report
Table 107. Key Data Information from Secondary Sources
Table 108. Key Data Information from Primary Sources
Table 109. Authors List of This Report
List of Figures
Figure 1. Orphan Diseases Picture
Figure 2. Global Orphan Diseases Market Size Comparison by Therapy Area Type (2020-2031) & (US$ Million)
Figure 3. Global Orphan Diseases Market Share by Therapy Area Type: 2024 VS 2031
Figure 4. Ocology Features
Figure 5. Hematology Features
Figure 6. Neurology Features
Figure 7. Endocrinology Features
Figure 8. Cardiovascular Features
Figure 9. Respiratory Features
Figure 10. Immunotherapy Features
Figure 11. Others Features
Figure 12. Global Orphan Diseases Market Size by Application (2020-2031) & (US$ Million)
Figure 13. Global Orphan Diseases Market Share by Application: 2024 VS 2031
Figure 14. Hospital Pharmacy Case Studies
Figure 15. Retail Pharmacy Case Studies
Figure 16. Others Case Studies
Figure 17. Orphan Diseases Report Years Considered
Figure 18. Global Orphan Diseases Market Size (US$ Million), Year-over-Year: 2020-2031
Figure 19. Global Orphan Diseases Market Size, (US$ Million), 2020 VS 2024 VS 2031
Figure 20. Global Orphan Diseases Market Share by Region: 2024 VS 2031
Figure 21. Global Orphan Diseases Market Share by Players in 2024
Figure 22. Global Top Orphan Diseases Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Orphan Diseases as of 2024)
Figure 23. The Top 10 and 5 Players Market Share by Orphan Diseases Revenue in 2024
Figure 24. North America Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 25. North America Orphan Diseases Market Share by Country (2020-2031)
Figure 26. United States Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 27. Canada Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 28. Europe Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 29. Europe Orphan Diseases Market Share by Country (2020-2031)
Figure 30. Germany Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 31. France Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 32. U.K. Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 33. Italy Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 34. Russia Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 35. Nordic Countries Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 36. Asia-Pacific Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 37. Asia-Pacific Orphan Diseases Market Share by Region (2020-2031)
Figure 38. China Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 39. Japan Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 40. South Korea Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 41. Southeast Asia Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 42. India Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 43. Australia Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 44. Latin America Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 45. Latin America Orphan Diseases Market Share by Country (2020-2031)
Figure 46. Mexico Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 47. Brazil Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 48. Middle East & Africa Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 49. Middle East & Africa Orphan Diseases Market Share by Country (2020-2031)
Figure 50. Turkey Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 51. Saudi Arabia Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 52. UAE Orphan Diseases Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 53. Bristol-Myers Squibb Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 54. Novartis Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 55. Celgene Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 56. Roche Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 57. Pfizer Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 58. Alexion Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 59. Sanofi Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 60. Vertex Pharmaceuticals Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 61. GlaxoSmithKline Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 62. Merck Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 63. Abbvie Revenue Growth Rate in Orphan Diseases Business (2020-2025)
Figure 64. Bottom-up and Top-down Approaches for This Report
Figure 65. Data Triangulation
Figure 66. Key Executives Interviewed