List of Tables
Table 1. Global Batten Disease Drug Pipeline Market Size Growth Rate by Type (US$ Million): 2020 VS 2024 VS 2031
Table 2. Key Players of Gene Drugs
Table 3. Key Players of Stem Cell Drugs
Table 4. Global Batten Disease Drug Pipeline Market Size Growth by Application (US$ Million): 2020 VS 2024 VS 2031
Table 5. Global Batten Disease Drug Pipeline Market Size by Region (US$ Million): 2020 VS 2024 VS 2031
Table 6. Global Batten Disease Drug Pipeline Market Size by Region (2020-2025) & (US$ Million)
Table 7. Global Batten Disease Drug Pipeline Market Share by Region (2020-2025)
Table 8. Global Batten Disease Drug Pipeline Forecasted Market Size by Region (2026-2031) & (US$ Million)
Table 9. Global Batten Disease Drug Pipeline Market Share by Region (2026-2031)
Table 10. Batten Disease Drug Pipeline Market Trends
Table 11. Batten Disease Drug Pipeline Market Drivers
Table 12. Batten Disease Drug Pipeline Market Challenges
Table 13. Batten Disease Drug Pipeline Market Restraints
Table 14. Global Batten Disease Drug Pipeline Revenue by Players (2020-2025) & (US$ Million)
Table 15. Global Batten Disease Drug Pipeline Market Share by Players (2020-2025)
Table 16. Global Top Batten Disease Drug Pipeline Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Batten Disease Drug Pipeline as of 2024)
Table 17. Ranking of Global Top Batten Disease Drug Pipeline Companies by Revenue (US$ Million) in 2024
Table 18. Global 5 Largest Players Market Share by Batten Disease Drug Pipeline Revenue (CR5 and HHI) & (2020-2025)
Table 19. Global Key Players of Batten Disease Drug Pipeline, Headquarters and Area Served
Table 20. Global Key Players of Batten Disease Drug Pipeline, Product and Application
Table 21. Global Key Players of Batten Disease Drug Pipeline, Date of Enter into This Industry
Table 22. Mergers & Acquisitions, Expansion Plans
Table 23. Global Batten Disease Drug Pipeline Market Size by Type (2020-2025) & (US$ Million)
Table 24. Global Batten Disease Drug Pipeline Revenue Market Share by Type (2020-2025)
Table 25. Global Batten Disease Drug Pipeline Forecasted Market Size by Type (2026-2031) & (US$ Million)
Table 26. Global Batten Disease Drug Pipeline Revenue Market Share by Type (2026-2031)
Table 27. Global Batten Disease Drug Pipeline Market Size by Application (2020-2025) & (US$ Million)
Table 28. Global Batten Disease Drug Pipeline Revenue Market Share by Application (2020-2025)
Table 29. Global Batten Disease Drug Pipeline Forecasted Market Size by Application (2026-2031) & (US$ Million)
Table 30. Global Batten Disease Drug Pipeline Revenue Market Share by Application (2026-2031)
Table 31. North America Batten Disease Drug Pipeline Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 32. North America Batten Disease Drug Pipeline Market Size by Country (2020-2025) & (US$ Million)
Table 33. North America Batten Disease Drug Pipeline Market Size by Country (2026-2031) & (US$ Million)
Table 34. Europe Batten Disease Drug Pipeline Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 35. Europe Batten Disease Drug Pipeline Market Size by Country (2020-2025) & (US$ Million)
Table 36. Europe Batten Disease Drug Pipeline Market Size by Country (2026-2031) & (US$ Million)
Table 37. Asia-Pacific Batten Disease Drug Pipeline Market Size Growth Rate by Region (US$ Million): 2020 VS 2024 VS 2031
Table 38. Asia-Pacific Batten Disease Drug Pipeline Market Size by Region (2020-2025) & (US$ Million)
Table 39. Asia-Pacific Batten Disease Drug Pipeline Market Size by Region (2026-2031) & (US$ Million)
Table 40. Latin America Batten Disease Drug Pipeline Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 41. Latin America Batten Disease Drug Pipeline Market Size by Country (2020-2025) & (US$ Million)
Table 42. Latin America Batten Disease Drug Pipeline Market Size by Country (2026-2031) & (US$ Million)
Table 43. Middle East & Africa Batten Disease Drug Pipeline Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 44. Middle East & Africa Batten Disease Drug Pipeline Market Size by Country (2020-2025) & (US$ Million)
Table 45. Middle East & Africa Batten Disease Drug Pipeline Market Size by Country (2026-2031) & (US$ Million)
Table 46. Abeona Therapeutics Inc Company Details
Table 47. Abeona Therapeutics Inc Business Overview
Table 48. Abeona Therapeutics Inc Batten Disease Drug Pipeline Product
Table 49. Abeona Therapeutics Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 50. Abeona Therapeutics Inc Recent Development
Table 51. Amicus Therapeutics Company Details
Table 52. Amicus Therapeutics Business Overview
Table 53. Amicus Therapeutics Batten Disease Drug Pipeline Product
Table 54. Amicus Therapeutics Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 55. Amicus Therapeutics Recent Development
Table 56. Blue Turtle Bio Technologies Inc Company Details
Table 57. Blue Turtle Bio Technologies Inc Business Overview
Table 58. Blue Turtle Bio Technologies Inc Batten Disease Drug Pipeline Product
Table 59. Blue Turtle Bio Technologies Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 60. Blue Turtle Bio Technologies Inc Recent Development
Table 61. Circumvent Pharmaceuticals Inc Company Details
Table 62. Circumvent Pharmaceuticals Inc Business Overview
Table 63. Circumvent Pharmaceuticals Inc Batten Disease Drug Pipeline Product
Table 64. Circumvent Pharmaceuticals Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 65. Circumvent Pharmaceuticals Inc Recent Development
Table 66. Collaborations Pharmaceuticals Inc Company Details
Table 67. Collaborations Pharmaceuticals Inc Business Overview
Table 68. Collaborations Pharmaceuticals Inc Batten Disease Drug Pipeline Product
Table 69. Collaborations Pharmaceuticals Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 70. Collaborations Pharmaceuticals Inc Recent Development
Table 71. Exicure Inc Company Details
Table 72. Exicure Inc Business Overview
Table 73. Exicure Inc Batten Disease Drug Pipeline Product
Table 74. Exicure Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 75. Exicure Inc Recent Development
Table 76. Polaryx Therapeutics Inc Company Details
Table 77. Polaryx Therapeutics Inc Business Overview
Table 78. Polaryx Therapeutics Inc Batten Disease Drug Pipeline Product
Table 79. Polaryx Therapeutics Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 80. Polaryx Therapeutics Inc Recent Development
Table 81. RegenxBio Inc Company Details
Table 82. RegenxBio Inc Business Overview
Table 83. RegenxBio Inc Batten Disease Drug Pipeline Product
Table 84. RegenxBio Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 85. RegenxBio Inc Recent Development
Table 86. Retrotope Inc Company Details
Table 87. Retrotope Inc Business Overview
Table 88. Retrotope Inc Batten Disease Drug Pipeline Product
Table 89. Retrotope Inc Revenue in Batten Disease Drug Pipeline Business (2020-2025) & (US$ Million)
Table 90. Retrotope Inc Recent Development
Table 91. Research Programs/Design for This Report
Table 92. Key Data Information from Secondary Sources
Table 93. Key Data Information from Primary Sources
Table 94. Authors List of This Report
List of Figures
Figure 1. Batten Disease Drug Pipeline Picture
Figure 2. Global Batten Disease Drug Pipeline Market Size Comparison by Type (2020-2031) & (US$ Million)
Figure 3. Global Batten Disease Drug Pipeline Market Share by Type: 2024 VS 2031
Figure 4. Gene Drugs Features
Figure 5. Stem Cell Drugs Features
Figure 6. Global Batten Disease Drug Pipeline Market Size by Application (2020-2031) & (US$ Million)
Figure 7. Global Batten Disease Drug Pipeline Market Share by Application: 2024 VS 2031
Figure 8. Hospital and Clinics Case Studies
Figure 9. Specialty Centers Case Studies
Figure 10. Batten Disease Drug Pipeline Report Years Considered
Figure 11. Global Batten Disease Drug Pipeline Market Size (US$ Million), Year-over-Year: 2020-2031
Figure 12. Global Batten Disease Drug Pipeline Market Size, (US$ Million), 2020 VS 2024 VS 2031
Figure 13. Global Batten Disease Drug Pipeline Market Share by Region: 2024 VS 2031
Figure 14. Global Batten Disease Drug Pipeline Market Share by Players in 2024
Figure 15. Global Top Batten Disease Drug Pipeline Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Batten Disease Drug Pipeline as of 2024)
Figure 16. The Top 10 and 5 Players Market Share by Batten Disease Drug Pipeline Revenue in 2024
Figure 17. North America Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 18. North America Batten Disease Drug Pipeline Market Share by Country (2020-2031)
Figure 19. United States Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 20. Canada Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 21. Europe Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 22. Europe Batten Disease Drug Pipeline Market Share by Country (2020-2031)
Figure 23. Germany Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 24. France Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 25. U.K. Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 26. Italy Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 27. Russia Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 28. Nordic Countries Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 29. Asia-Pacific Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 30. Asia-Pacific Batten Disease Drug Pipeline Market Share by Region (2020-2031)
Figure 31. China Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 32. Japan Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 33. South Korea Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 34. Southeast Asia Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 35. India Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 36. Australia Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 37. Latin America Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 38. Latin America Batten Disease Drug Pipeline Market Share by Country (2020-2031)
Figure 39. Mexico Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 40. Brazil Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 41. Middle East & Africa Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 42. Middle East & Africa Batten Disease Drug Pipeline Market Share by Country (2020-2031)
Figure 43. Turkey Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 44. Saudi Arabia Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 45. UAE Batten Disease Drug Pipeline Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 46. Abeona Therapeutics Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 47. Amicus Therapeutics Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 48. Blue Turtle Bio Technologies Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 49. Circumvent Pharmaceuticals Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 50. Collaborations Pharmaceuticals Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 51. Exicure Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 52. Polaryx Therapeutics Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 53. RegenxBio Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 54. Retrotope Inc Revenue Growth Rate in Batten Disease Drug Pipeline Business (2020-2025)
Figure 55. Bottom-up and Top-down Approaches for This Report
Figure 56. Data Triangulation
Figure 57. Key Executives Interviewed