Global Gene Therapy for Mucopolysaccharidosis Market Research Report 2022

Market Analysis and Insights: Global Gene Therapy for Mucopolysaccharidosis Market

Mucopolysaccharidosis consists of a group of more than 40 genetic disorders that forms a part of lysosomal storage disease. They are caused by an inherited deficiency of an enzyme involved in the degradation of acid glycosaminoglycans (GAGs), which was previously known as mucopolysaccharidosis. All of the mucopolysaccharidoses are rare, autosomal recessive, except for mucopolysaccharidosis III, as it is X-linked.

The global Gene Therapy for Mucopolysaccharidosis market size is projected to reach US$ million by 2028, from US$ million in 2021, at a CAGR of % during 2022-2028.

Over the past few years, gene therapy has emerged as one of the most exciting approaches for the treatment of mucopolysaccharidosis. One of the promising therapy is replacement gene therapy, which replaces faulty genes with normal ones in the body. It is considered to be a potential cure to mucopolysaccharidoses and a promising option in the long run.

With industry-standard accuracy in analysis and high data integrity, the report makes a brilliant attempt to unveil key opportunities available in the global Gene Therapy for Mucopolysaccharidosis market to help players in achieving a strong market position. Buyers of the report can access verified and reliable market forecasts, including those for the overall size of the global Gene Therapy for Mucopolysaccharidosis market in terms of revenue.

Overall, the report proves to be an effective tool that players can use to gain a competitive edge over their competitors and ensure lasting success in the global Gene Therapy for Mucopolysaccharidosis market. All of the findings, data, and information provided in the report are validated and revalidated with the help of trustworthy sources. The analysts who have authored the report took a unique and industry-best research and analysis approach for an in-depth study of the global Gene Therapy for Mucopolysaccharidosis market.

Global Gene Therapy for Mucopolysaccharidosis Scope and Market Size

Gene Therapy for Mucopolysaccharidosis market is segmented by players, region (country), by Type and by Application. Players, stakeholders, and other participants in the global Gene Therapy for Mucopolysaccharidosis market will be able to gain the upper hand as they use the report as a powerful resource. The segmental analysis focuses on revenue and forecast by Type and by Application for the period 2017-2028.

Intravenous

ICV

Intracerebral

Intracisternal

Mucopolysaccharidosis I

Mucopolysaccharidosis II

Mucopolysaccharidosis III A

Mucopolysaccharidosis III B

North America

United States

Canada

Europe

Germany

France

UK

Italy

Russia

Nordic Countries

Rest of Europe

Asia-Pacific

China

Japan

South Korea

Southeast Asia

India

Australia

Rest of Asia

Latin America

Mexico

Brazil

Rest of Latin America

Middle East & Africa

Turkey

Saudi Arabia

UAE

Rest of MEA

Sangamo Therapeutics

Swedish Orphan Biovitrum

uniQure

1.1 Study Scope

1.2 Market Analysis by Type

1.2.1 Global Gene Therapy for Mucopolysaccharidosis Market Size Growth Rate by Type: 2017 VS 2021 VS 2028

1.2.2 Intravenous

1.2.3 ICV

1.2.4 Intracerebral

1.2.5 Intracisternal

1.3 Market by Application

1.3.1 Global Gene Therapy for Mucopolysaccharidosis Market Share by Application: 2017 VS 2021 VS 2028

1.3.2 Mucopolysaccharidosis I

1.3.3 Mucopolysaccharidosis II

1.3.4 Mucopolysaccharidosis III A

1.3.5 Mucopolysaccharidosis III B

1.4 Study Objectives

1.5 Years Considered

2.1 Global Gene Therapy for Mucopolysaccharidosis Market Perspective (2017-2028)

2.2 Gene Therapy for Mucopolysaccharidosis Growth Trends by Region

2.2.1 Gene Therapy for Mucopolysaccharidosis Market Size by Region: 2017 VS 2021 VS 2028

2.2.2 Gene Therapy for Mucopolysaccharidosis Historic Market Size by Region (2017-2022)

2.2.3 Gene Therapy for Mucopolysaccharidosis Forecasted Market Size by Region (2023-2028)

2.3 Gene Therapy for Mucopolysaccharidosis Market Dynamics

2.3.1 Gene Therapy for Mucopolysaccharidosis Industry Trends

2.3.2 Gene Therapy for Mucopolysaccharidosis Market Drivers

2.3.3 Gene Therapy for Mucopolysaccharidosis Market Challenges

2.3.4 Gene Therapy for Mucopolysaccharidosis Market Restraints

3.1 Global Top Gene Therapy for Mucopolysaccharidosis Players by Revenue

3.1.1 Global Top Gene Therapy for Mucopolysaccharidosis Players by Revenue (2017-2022)

3.1.2 Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Players (2017-2022)

3.2 Global Gene Therapy for Mucopolysaccharidosis Market Share by Company Type (Tier 1, Tier 2, and Tier 3)

3.3 Players Covered: Ranking by Gene Therapy for Mucopolysaccharidosis Revenue

3.4 Global Gene Therapy for Mucopolysaccharidosis Market Concentration Ratio

3.4.1 Global Gene Therapy for Mucopolysaccharidosis Market Concentration Ratio (CR5 and HHI)

3.4.2 Global Top 10 and Top 5 Companies by Gene Therapy for Mucopolysaccharidosis Revenue in 2021

3.5 Gene Therapy for Mucopolysaccharidosis Key Players Head office and Area Served

3.6 Key Players Gene Therapy for Mucopolysaccharidosis Product Solution and Service

3.7 Date of Enter into Gene Therapy for Mucopolysaccharidosis Market

3.8 Mergers & Acquisitions, Expansion Plans

4.1 Global Gene Therapy for Mucopolysaccharidosis Historic Market Size by Type (2017-2022)

4.2 Global Gene Therapy for Mucopolysaccharidosis Forecasted Market Size by Type (2023-2028)

5.1 Global Gene Therapy for Mucopolysaccharidosis Historic Market Size by Application (2017-2022)

5.2 Global Gene Therapy for Mucopolysaccharidosis Forecasted Market Size by Application (2023-2028)

6.1 North America Gene Therapy for Mucopolysaccharidosis Market Size (2017-2028)

6.2 North America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022)

6.3 North America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028)

6.4 United States

6.5 Canada

7.1 Europe Gene Therapy for Mucopolysaccharidosis Market Size (2017-2028)

7.2 Europe Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022)

7.3 Europe Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028)

7.4 Germany

7.5 France

7.6 U.K.

7.7 Italy

7.8 Russia

7.9 Nordic Countries

8.1 Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Size (2017-2028)

8.2 Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022)

8.3 Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028)

8.4 China

8.5 Japan

8.6 South Korea

8.7 Southeast Asia

8.8 India

8.9 Australia

9.1 Latin America Gene Therapy for Mucopolysaccharidosis Market Size (2017-2028)

9.2 Latin America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022)

9.3 Latin America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028)

9.4 Mexico

9.5 Brazil

10.1 Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Size (2017-2028)

10.2 Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022)

10.3 Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028)

10.4 Turkey

10.5 Saudi Arabia

10.6 UAE

11.1 Sangamo Therapeutics

11.1.1 Sangamo Therapeutics Company Detail

11.1.2 Sangamo Therapeutics Business Overview

11.1.3 Sangamo Therapeutics Gene Therapy for Mucopolysaccharidosis Introduction

11.1.4 Sangamo Therapeutics Revenue in Gene Therapy for Mucopolysaccharidosis Business (2017-2022)

11.1.5 Sangamo Therapeutics Recent Development

11.2 Swedish Orphan Biovitrum

11.2.1 Swedish Orphan Biovitrum Company Detail

11.2.2 Swedish Orphan Biovitrum Business Overview

11.2.3 Swedish Orphan Biovitrum Gene Therapy for Mucopolysaccharidosis Introduction

11.2.4 Swedish Orphan Biovitrum Revenue in Gene Therapy for Mucopolysaccharidosis Business (2017-2022)

11.2.5 Swedish Orphan Biovitrum Recent Development

11.3 uniQure

11.3.1 uniQure Company Detail

11.3.2 uniQure Business Overview

11.3.3 uniQure Gene Therapy for Mucopolysaccharidosis Introduction

11.3.4 uniQure Revenue in Gene Therapy for Mucopolysaccharidosis Business (2017-2022)

11.3.5 uniQure Recent Development

13.1 Research Methodology

13.1.1 Methodology/Research Approach

13.1.2 Data Source

13.2 Disclaimer

13.3 Author Details

List of Tables

    Table 1. Global Gene Therapy for Mucopolysaccharidosis Market Size Growth Rate by Type (US$ Million): 2017 VS 2021 VS 2028

    Table 2. Key Players of Intravenous

    Table 3. Key Players of ICV

    Table 4. Key Players of Intracerebral

    Table 5. Key Players of Intracisternal

    Table 6. Global Gene Therapy for Mucopolysaccharidosis Market Size Growth by Application (US$ Million): 2017 VS 2021 VS 2028

    Table 7. Global Gene Therapy for Mucopolysaccharidosis Market Size by Region (US$ Million): 2017 VS 2021 VS 2028

    Table 8. Global Gene Therapy for Mucopolysaccharidosis Market Size by Region (2017-2022) & (US$ Million)

    Table 9. Global Gene Therapy for Mucopolysaccharidosis Market Share by Region (2017-2022)

    Table 10. Global Gene Therapy for Mucopolysaccharidosis Forecasted Market Size by Region (2023-2028) & (US$ Million)

    Table 11. Global Gene Therapy for Mucopolysaccharidosis Market Share by Region (2023-2028)

    Table 12. Gene Therapy for Mucopolysaccharidosis Market Trends

    Table 13. Gene Therapy for Mucopolysaccharidosis Market Drivers

    Table 14. Gene Therapy for Mucopolysaccharidosis Market Challenges

    Table 15. Gene Therapy for Mucopolysaccharidosis Market Restraints

    Table 16. Global Gene Therapy for Mucopolysaccharidosis Revenue by Players (2017-2022) & (US$ Million)

    Table 17. Global Gene Therapy for Mucopolysaccharidosis Market Share by Players (2017-2022)

    Table 18. Global Top Gene Therapy for Mucopolysaccharidosis Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Gene Therapy for Mucopolysaccharidosis as of 2021)

    Table 19. Ranking of Global Top Gene Therapy for Mucopolysaccharidosis Companies by Revenue (US$ Million) in 2021

    Table 20. Global 5 Largest Players Market Share by Gene Therapy for Mucopolysaccharidosis Revenue (CR5 and HHI) & (2017-2022)

    Table 21. Key Players Headquarters and Area Served

    Table 22. Key Players Gene Therapy for Mucopolysaccharidosis Product Solution and Service

    Table 23. Date of Enter into Gene Therapy for Mucopolysaccharidosis Market

    Table 24. Mergers & Acquisitions, Expansion Plans

    Table 25. Global Gene Therapy for Mucopolysaccharidosis Market Size by Type (2017-2022) & (US$ Million)

    Table 26. Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Type (2017-2022)

    Table 27. Global Gene Therapy for Mucopolysaccharidosis Forecasted Market Size by Type (2023-2028) & (US$ Million)

    Table 28. Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Type (2023-2028)

    Table 29. Global Gene Therapy for Mucopolysaccharidosis Market Size by Application (2017-2022) & (US$ Million)

    Table 30. Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Application (2017-2022)

    Table 31. Global Gene Therapy for Mucopolysaccharidosis Forecasted Market Size by Application (2023-2028) & (US$ Million)

    Table 32. Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Application (2023-2028)

    Table 33. North America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022) & (US$ Million)

    Table 34. North America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028) & (US$ Million)

    Table 35. Europe Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022) & (US$ Million)

    Table 36. Europe Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028) & (US$ Million)

    Table 37. Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Size by Region (2017-2022) & (US$ Million)

    Table 38. Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Size by Region (2023-2028) & (US$ Million)

    Table 39. Latin America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022) & (US$ Million)

    Table 40. Latin America Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028) & (US$ Million)

    Table 41. Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Size by Country (2017-2022) & (US$ Million)

    Table 42. Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Size by Country (2023-2028) & (US$ Million)

    Table 43. Sangamo Therapeutics Company Detail

    Table 44. Sangamo Therapeutics Business Overview

    Table 45. Sangamo Therapeutics Gene Therapy for Mucopolysaccharidosis Product

    Table 46. Sangamo Therapeutics Revenue in Gene Therapy for Mucopolysaccharidosis Business (2017-2022) & (US$ Million)

    Table 47. Sangamo Therapeutics Recent Development

    Table 48. Swedish Orphan Biovitrum Company Detail

    Table 49. Swedish Orphan Biovitrum Business Overview

    Table 50. Swedish Orphan Biovitrum Gene Therapy for Mucopolysaccharidosis Product

    Table 51. Swedish Orphan Biovitrum Revenue in Gene Therapy for Mucopolysaccharidosis Business (2017-2022) & (US$ Million)

    Table 52. Swedish Orphan Biovitrum Recent Development

    Table 53. uniQure Company Detail

    Table 54. uniQure Business Overview

    Table 55. uniQure Gene Therapy for Mucopolysaccharidosis Product

    Table 56. uniQure Revenue in Gene Therapy for Mucopolysaccharidosis Business (2017-2022) & (US$ Million)

    Table 57. uniQure Recent Development

    Table 58. Research Programs/Design for This Report

    Table 59. Key Data Information from Secondary Sources

    Table 60. Key Data Information from Primary Sources

List of Figures

    Figure 1. Global Gene Therapy for Mucopolysaccharidosis Market Share by Type: 2021 VS 2028

    Figure 2. Intravenous Features

    Figure 3. ICV Features

    Figure 4. Intracerebral Features

    Figure 5. Intracisternal Features

    Figure 6. Global Gene Therapy for Mucopolysaccharidosis Market Share by Application in 2021 & 2028

    Figure 7. Mucopolysaccharidosis I Case Studies

    Figure 8. Mucopolysaccharidosis II Case Studies

    Figure 9. Mucopolysaccharidosis III A Case Studies

    Figure 10. Mucopolysaccharidosis III B Case Studies

    Figure 11. Gene Therapy for Mucopolysaccharidosis Report Years Considered

    Figure 12. Global Gene Therapy for Mucopolysaccharidosis Market Size (US$ Million), Year-over-Year: 2017-2028

    Figure 13. Global Gene Therapy for Mucopolysaccharidosis Market Size, (US$ Million), 2017 VS 2021 VS 2028

    Figure 14. Global Gene Therapy for Mucopolysaccharidosis Market Share by Region: 2021 VS 2028

    Figure 15. Global Gene Therapy for Mucopolysaccharidosis Market Share by Players in 2021

    Figure 16. Global Top Gene Therapy for Mucopolysaccharidosis Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Gene Therapy for Mucopolysaccharidosis as of 2021)

    Figure 17. The Top 10 and 5 Players Market Share by Gene Therapy for Mucopolysaccharidosis Revenue in 2021

    Figure 18. North America Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 19. North America Gene Therapy for Mucopolysaccharidosis Market Share by Country (2017-2028)

    Figure 20. United States Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 21. Canada Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 22. Europe Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 23. Europe Gene Therapy for Mucopolysaccharidosis Market Share by Country (2017-2028)

    Figure 24. Germany Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 25. France Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 26. U.K. Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 27. Italy Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 28. Russia Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 29. Nordic Countries Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 30. Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 31. Asia-Pacific Gene Therapy for Mucopolysaccharidosis Market Share by Region (2017-2028)

    Figure 32. China Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 33. Japan Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 34. South Korea Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 35. Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 36. India Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 37. Australia Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 38. Latin America Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 39. Latin America Gene Therapy for Mucopolysaccharidosis Market Share by Country (2017-2028)

    Figure 40. Mexico Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 41. Brazil Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 42. Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 43. Middle East & Africa Gene Therapy for Mucopolysaccharidosis Market Share by Country (2017-2028)

    Figure 44. Turkey Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 45. Saudi Arabia Gene Therapy for Mucopolysaccharidosis Market Size YoY Growth (2017-2028) & (US$ Million)

    Figure 46. Sangamo Therapeutics Revenue Growth Rate in Gene Therapy for Mucopolysaccharidosis Business (2017-2022)

    Figure 47. Swedish Orphan Biovitrum Revenue Growth Rate in Gene Therapy for Mucopolysaccharidosis Business (2017-2022)

    Figure 48. uniQure Revenue Growth Rate in Gene Therapy for Mucopolysaccharidosis Business (2017-2022)

    Figure 49. Bottom-up and Top-down Approaches for This Report

    Figure 50. Data Triangulation

    Figure 51. Key Executives Interviewed