List of Tables
Table 1. Batten Disease Treatment Market Trends
Table 2. Batten Disease Treatment Market Drivers & Opportunity
Table 3. Batten Disease Treatment Market Challenges
Table 4. Batten Disease Treatment Market Restraints
Table 5. Global Batten Disease Treatment Revenue by Company (2019-2024) & (US$ Million)
Table 6. Global Batten Disease Treatment Revenue Market Share by Company (2019-2024)
Table 7. Key Companies Batten Disease Treatment Manufacturing Base Distribution and Headquarters
Table 8. Key Companies Batten Disease Treatment Product Type
Table 9. Key Companies Time to Begin Mass Production of Batten Disease Treatment
Table 10. Global Batten Disease Treatment Companies Market Concentration Ratio (CR5 and HHI)
Table 11. Global Top Companies Market Share by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Batten Disease Treatment as of 2023)
Table 12. Mergers & Acquisitions, Expansion Plans
Table 13. Global Batten Disease Treatment Sales Value by Type: 2019 VS 2023 VS 2030 (US$ Million)
Table 14. Global Batten Disease Treatment Sales Value by Type (2019-2024) & (US$ Million)
Table 15. Global Batten Disease Treatment Sales Value by Type (2025-2030) & (US$ Million)
Table 16. Global Batten Disease Treatment Sales Market Share in Value by Type (2019-2024) & (%)
Table 17. Global Batten Disease Treatment Sales Market Share in Value by Type (2025-2030) & (%)
Table 18. Global Batten Disease Treatment Sales Value by Application: 2019 VS 2023 VS 2030 (US$ Million)
Table 19. Global Batten Disease Treatment Sales Value by Application (2019-2024) & (US$ Million)
Table 20. Global Batten Disease Treatment Sales Value by Application (2025-2030) & (US$ Million)
Table 21. Global Batten Disease Treatment Sales Market Share in Value by Application (2019-2024) & (%)
Table 22. Global Batten Disease Treatment Sales Market Share in Value by Application (2025-2030) & (%)
Table 23. Global Batten Disease Treatment Sales Value by Region: 2019 VS 2023 VS 2030 (US$ Million)
Table 24. Global Batten Disease Treatment Sales Value by Region (2019-2024) & (US$ Million)
Table 25. Global Batten Disease Treatment Sales Value by Region (2025-2030) & (US$ Million)
Table 26. Global Batten Disease Treatment Sales Value by Region (2019-2024) & (%)
Table 27. Global Batten Disease Treatment Sales Value by Region (2025-2030) & (%)
Table 28. Key Countries/Regions Batten Disease Treatment Sales Value Growth Trends, (US$ Million): 2019 VS 2023 VS 2030
Table 29. Key Countries/Regions Batten Disease Treatment Sales Value, (2019-2024) & (US$ Million)
Table 30. Key Countries/Regions Batten Disease Treatment Sales Value, (2025-2030) & (US$ Million)
Table 31. BioMarin Pharmaceuticals Basic Information List
Table 32. BioMarin Pharmaceuticals Description and Business Overview
Table 33. BioMarin Pharmaceuticals Batten Disease Treatment Products, Services and Solutions
Table 34. Revenue (US$ Million) in Batten Disease Treatment Business of BioMarin Pharmaceuticals (2019-2024)
Table 35. BioMarin Pharmaceuticals Recent Developments
Table 36. Seneb BioSciences, Inc. Basic Information List
Table 37. Seneb BioSciences, Inc. Description and Business Overview
Table 38. Seneb BioSciences, Inc. Batten Disease Treatment Products, Services and Solutions
Table 39. Revenue (US$ Million) in Batten Disease Treatment Business of Seneb BioSciences, Inc. (2019-2024)
Table 40. Seneb BioSciences, Inc. Recent Developments
Table 41. ReGenX Biosciences LLC Basic Information List
Table 42. ReGenX Biosciences LLC Description and Business Overview
Table 43. ReGenX Biosciences LLC Batten Disease Treatment Products, Services and Solutions
Table 44. Revenue (US$ Million) in Batten Disease Treatment Business of ReGenX Biosciences LLC (2019-2024)
Table 45. ReGenX Biosciences LLC Recent Developments
Table 46. Amicus Therapeutics Basic Information List
Table 47. Amicus Therapeutics Description and Business Overview
Table 48. Amicus Therapeutics Batten Disease Treatment Products, Services and Solutions
Table 49. Revenue (US$ Million) in Batten Disease Treatment Business of Amicus Therapeutics (2019-2024)
Table 50. Amicus Therapeutics Recent Developments
Table 51. Ionis Pharmaceuticals, Inc. Basic Information List
Table 52. Ionis Pharmaceuticals, Inc. Description and Business Overview
Table 53. Ionis Pharmaceuticals, Inc. Batten Disease Treatment Products, Services and Solutions
Table 54. Revenue (US$ Million) in Batten Disease Treatment Business of Ionis Pharmaceuticals, Inc. (2019-2024)
Table 55. Ionis Pharmaceuticals, Inc. Recent Developments
Table 56. Celenex, Inc. Basic Information List
Table 57. Celenex, Inc. Description and Business Overview
Table 58. Celenex, Inc. Batten Disease Treatment Products, Services and Solutions
Table 59. Revenue (US$ Million) in Batten Disease Treatment Business of Celenex, Inc. (2019-2024)
Table 60. Celenex, Inc. Recent Developments
Table 61. Key Raw Materials Lists
Table 62. Raw Materials Key Suppliers Lists
Table 63. Batten Disease Treatment Downstream Customers
Table 64. Batten Disease Treatment Distributors List
Table 65. Research Programs/Design for This Report
Table 66. Key Data Information from Secondary Sources
Table 67. Key Data Information from Primary Sources
Table 68. Business Unit and Senior & Team Lead Analysts
List of Figures
Figure 1. Batten Disease Treatment Product Picture
Figure 2. Global Batten Disease Treatment Sales Value, 2019 VS 2023 VS 2030 (US$ Million)
Figure 3. Global Batten Disease Treatment Sales Value (2019-2030) & (US$ Million)
Figure 4. Batten Disease Treatment Report Years Considered
Figure 5. Global Batten Disease Treatment Players Revenue Ranking (2023) & (US$ Million)
Figure 6. The 5 and 10 Largest Manufacturers in the World: Market Share by Batten Disease Treatment Revenue in 2023
Figure 7. Batten Disease Treatment Market Share by Company Type (Tier 1, Tier 2, and Tier 3): 2019 VS 2023
Figure 8. Occupational Therapies Picture
Figure 9. Physical Therapies Picture
Figure 10. Global Batten Disease Treatment Sales Value by Type (2019 VS 2023 VS 2030) & (US$ Million)
Figure 11. Global Batten Disease Treatment Sales Value Market Share by Type, 2023 & 2030
Figure 12. Product Picture of Infantile NCL
Figure 13. Product Picture of Late Infantile NCL
Figure 14. Product Picture of Juvenile NCL
Figure 15. Product Picture of Adult NCL
Figure 16. Global Batten Disease Treatment Sales Value by Application (2019 VS 2023 VS 2030) & (US$ Million)
Figure 17. Global Batten Disease Treatment Sales Value Market Share by Application, 2023 & 2030
Figure 18. North America Batten Disease Treatment Sales Value (2019-2030) & (US$ Million)
Figure 19. North America Batten Disease Treatment Sales Value by Country (%), 2023 VS 2030
Figure 20. Europe Batten Disease Treatment Sales Value (2019-2030) & (US$ Million)
Figure 21. Europe Batten Disease Treatment Sales Value by Country (%), 2023 VS 2030
Figure 22. Asia Pacific Batten Disease Treatment Sales Value (2019-2030) & (US$ Million)
Figure 23. Asia Pacific Batten Disease Treatment Sales Value by Country (%), 2023 VS 2030
Figure 24. South America Batten Disease Treatment Sales Value (2019-2030) & (US$ Million)
Figure 25. South America Batten Disease Treatment Sales Value by Country (%), 2023 VS 2030
Figure 26. Middle East & Africa Batten Disease Treatment Sales Value (2019-2030) & (US$ Million)
Figure 27. Middle East & Africa Batten Disease Treatment Sales Value by Country (%), 2023 VS 2030
Figure 28. Key Countries/Regions Batten Disease Treatment Sales Value (%), (2019-2030)
Figure 29. United States Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 30. United States Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 31. United States Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 32. Europe Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 33. Europe Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 34. Europe Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 35. China Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 36. China Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 37. China Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 38. Japan Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 39. Japan Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 40. Japan Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 41. South Korea Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 42. South Korea Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 43. South Korea Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 44. Southeast Asia Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 45. Southeast Asia Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 46. Southeast Asia Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 47. India Batten Disease Treatment Sales Value, (2019-2030) & (US$ Million)
Figure 48. India Batten Disease Treatment Sales Value by Type (%), 2023 VS 2030
Figure 49. India Batten Disease Treatment Sales Value by Application (%), 2023 VS 2030
Figure 50. Batten Disease Treatment Industrial Chain
Figure 51. Batten Disease Treatment Manufacturing Cost Structure
Figure 52. Channels of Distribution (Direct Sales, and Distribution)
Figure 53. Bottom-up and Top-down Approaches for This Report
Figure 54. Data Triangulation