List of Tables
Table 1. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate by Type (US$ Million): 2020 VS 2024 VS 2031
Table 2. Key Players of Single-stranded AAV (ssAAV)
Table 3. Key Players of Self-complementary AAV (scAAV)
Table 4. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth by Application (US$ Million): 2020 VS 2024 VS 2031
Table 5. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (US$ Million): 2020 VS 2024 VS 2031
Table 6. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (2020-2025) & (US$ Million)
Table 7. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Region (2020-2025)
Table 8. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecasted Market Size by Region (2026-2031) & (US$ Million)
Table 9. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Region (2026-2031)
Table 10. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Trends
Table 11. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Drivers
Table 12. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Challenges
Table 13. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Restraints
Table 14. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue by Players (2020-2025) & (US$ Million)
Table 15. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Players (2020-2025)
Table 16. Global Top Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy as of 2024)
Table 17. Ranking of Global Top Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Companies by Revenue (US$ Million) in 2024
Table 18. Global 5 Largest Players Market Share by Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue (CR5 and HHI) & (2020-2025)
Table 19. Global Key Players of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy, Headquarters and Area Served
Table 20. Global Key Players of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy, Product and Application
Table 21. Global Key Players of Adeno-Associated Virus (AAV) Vector-Based Gene Therapy, Date of Enter into This Industry
Table 22. Mergers & Acquisitions, Expansion Plans
Table 23. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Type (2020-2025) & (US$ Million)
Table 24. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Type (2020-2025)
Table 25. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecasted Market Size by Type (2026-2031) & (US$ Million)
Table 26. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Type (2026-2031)
Table 27. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2020-2025) & (US$ Million)
Table 28. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Application (2020-2025)
Table 29. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Forecasted Market Size by Application (2026-2031) & (US$ Million)
Table 30. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue Market Share by Application (2026-2031)
Table 31. North America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 32. North America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2020-2025) & (US$ Million)
Table 33. North America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2026-2031) & (US$ Million)
Table 34. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 35. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2020-2025) & (US$ Million)
Table 36. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2026-2031) & (US$ Million)
Table 37. Asia-Pacific Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate by Region (US$ Million): 2020 VS 2024 VS 2031
Table 38. Asia-Pacific Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (2020-2025) & (US$ Million)
Table 39. Asia-Pacific Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Region (2026-2031) & (US$ Million)
Table 40. Latin America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 41. Latin America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2020-2025) & (US$ Million)
Table 42. Latin America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2026-2031) & (US$ Million)
Table 43. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 44. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2020-2025) & (US$ Million)
Table 45. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Country (2026-2031) & (US$ Million)
Table 46. BioMarin Pharmaceutical Company Details
Table 47. BioMarin Pharmaceutical Business Overview
Table 48. BioMarin Pharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 49. BioMarin Pharmaceutical Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 50. BioMarin Pharmaceutical Recent Development
Table 51. Sangamo Therapeutics Company Details
Table 52. Sangamo Therapeutics Business Overview
Table 53. Sangamo Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 54. Sangamo Therapeutics Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 55. Sangamo Therapeutics Recent Development
Table 56. Amicus Therapeutics Company Details
Table 57. Amicus Therapeutics Business Overview
Table 58. Amicus Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 59. Amicus Therapeutics Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 60. Amicus Therapeutics Recent Development
Table 61. Roche Company Details
Table 62. Roche Business Overview
Table 63. Roche Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 64. Roche Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 65. Roche Recent Development
Table 66. Pfizer Company Details
Table 67. Pfizer Business Overview
Table 68. Pfizer Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 69. Pfizer Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 70. Pfizer Recent Development
Table 71. NightstaRx Company Details
Table 72. NightstaRx Business Overview
Table 73. NightstaRx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 74. NightstaRx Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 75. NightstaRx Recent Development
Table 76. MeiraGTx Company Details
Table 77. MeiraGTx Business Overview
Table 78. MeiraGTx Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 79. MeiraGTx Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 80. MeiraGTx Recent Development
Table 81. Sarepta Therapeutics Company Details
Table 82. Sarepta Therapeutics Business Overview
Table 83. Sarepta Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 84. Sarepta Therapeutics Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 85. Sarepta Therapeutics Recent Development
Table 86. Neurocrine Biosciences Company Details
Table 87. Neurocrine Biosciences Business Overview
Table 88. Neurocrine Biosciences Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 89. Neurocrine Biosciences Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 90. Neurocrine Biosciences Recent Development
Table 91. Voyager Therapeutics Company Details
Table 92. Voyager Therapeutics Business Overview
Table 93. Voyager Therapeutics Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 94. Voyager Therapeutics Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 95. Voyager Therapeutics Recent Development
Table 96. Asklepios Biopharmaceutical Company Details
Table 97. Asklepios Biopharmaceutical Business Overview
Table 98. Asklepios Biopharmaceutical Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Product
Table 99. Asklepios Biopharmaceutical Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025) & (US$ Million)
Table 100. Asklepios Biopharmaceutical Recent Development
Table 101. Research Programs/Design for This Report
Table 102. Key Data Information from Secondary Sources
Table 103. Key Data Information from Primary Sources
Table 104. Authors List of This Report
List of Figures
Figure 1. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Picture
Figure 2. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size Comparison by Type (2020-2031) & (US$ Million)
Figure 3. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Type: 2024 VS 2031
Figure 4. Single-stranded AAV (ssAAV) Features
Figure 5. Self-complementary AAV (scAAV) Features
Figure 6. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size by Application (2020-2031) & (US$ Million)
Figure 7. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Application: 2024 VS 2031
Figure 8. Hemophilia Case Studies
Figure 9. Ophthalmology Case Studies
Figure 10. Lysosomal Storage Disorders Case Studies
Figure 11. Neurological Disorders Case Studies
Figure 12. Others Case Studies
Figure 13. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Report Years Considered
Figure 14. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size (US$ Million), Year-over-Year: 2020-2031
Figure 15. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size, (US$ Million), 2020 VS 2024 VS 2031
Figure 16. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Region: 2024 VS 2031
Figure 17. Global Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Players in 2024
Figure 18. Global Top Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy as of 2024)
Figure 19. The Top 10 and 5 Players Market Share by Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Revenue in 2024
Figure 20. North America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 21. North America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Country (2020-2031)
Figure 22. United States Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 23. Canada Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 24. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 25. Europe Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Country (2020-2031)
Figure 26. Germany Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 27. France Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 28. U.K. Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 29. Italy Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 30. Russia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 31. Nordic Countries Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 32. Asia-Pacific Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 33. Asia-Pacific Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Region (2020-2031)
Figure 34. China Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 35. Japan Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 36. South Korea Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 37. Southeast Asia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 38. India Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 39. Australia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 40. Latin America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 41. Latin America Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Country (2020-2031)
Figure 42. Mexico Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 43. Brazil Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 44. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 45. Middle East & Africa Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Share by Country (2020-2031)
Figure 46. Turkey Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 47. Saudi Arabia Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 48. UAE Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 49. BioMarin Pharmaceutical Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 50. Sangamo Therapeutics Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 51. Amicus Therapeutics Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 52. Roche Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 53. Pfizer Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 54. NightstaRx Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 55. MeiraGTx Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 56. Sarepta Therapeutics Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 57. Neurocrine Biosciences Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 58. Voyager Therapeutics Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 59. Asklepios Biopharmaceutical Revenue Growth Rate in Adeno-Associated Virus (AAV) Vector-Based Gene Therapy Business (2020-2025)
Figure 60. Bottom-up and Top-down Approaches for This Report
Figure 61. Data Triangulation
Figure 62. Key Executives Interviewed