List of Tables
Table 1. Global RNA-Targeted Small Molecule Drugs Market Size Growth Rate by Type (US$ Million): 2020 VS 2024 VS 2031
Table 2. Key Players of mRNA Translation Regulation
Table 3. Key Players of RNA Splicing Modification
Table 4. Key Players of Direct RNA Targeting
Table 5. Key Players of Indirect RNA Targeting - Epitranscriptomics
Table 6. Global RNA-Targeted Small Molecule Drugs Market Size Growth by Application (US$ Million): 2020 VS 2024 VS 2031
Table 7. Global RNA-Targeted Small Molecule Drugs Market Size by Region (US$ Million): 2020 VS 2024 VS 2031
Table 8. Global RNA-Targeted Small Molecule Drugs Market Size by Region (2020-2025) & (US$ Million)
Table 9. Global RNA-Targeted Small Molecule Drugs Market Share by Region (2020-2025)
Table 10. Global RNA-Targeted Small Molecule Drugs Forecasted Market Size by Region (2026-2031) & (US$ Million)
Table 11. Global RNA-Targeted Small Molecule Drugs Market Share by Region (2026-2031)
Table 12. RNA-Targeted Small Molecule Drugs Market Trends
Table 13. RNA-Targeted Small Molecule Drugs Market Drivers
Table 14. RNA-Targeted Small Molecule Drugs Market Challenges
Table 15. RNA-Targeted Small Molecule Drugs Market Restraints
Table 16. Global RNA-Targeted Small Molecule Drugs Revenue by Players (2020-2025) & (US$ Million)
Table 17. Global RNA-Targeted Small Molecule Drugs Market Share by Players (2020-2025)
Table 18. Global Top RNA-Targeted Small Molecule Drugs Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in RNA-Targeted Small Molecule Drugs as of 2024)
Table 19. Ranking of Global Top RNA-Targeted Small Molecule Drugs Companies by Revenue (US$ Million) in 2024
Table 20. Global 5 Largest Players Market Share by RNA-Targeted Small Molecule Drugs Revenue (CR5 and HHI) & (2020-2025)
Table 21. Global Key Players of RNA-Targeted Small Molecule Drugs, Headquarters and Area Served
Table 22. Global Key Players of RNA-Targeted Small Molecule Drugs, Product and Application
Table 23. Global Key Players of RNA-Targeted Small Molecule Drugs, Date of Enter into This Industry
Table 24. Mergers & Acquisitions, Expansion Plans
Table 25. Global RNA-Targeted Small Molecule Drugs Market Size by Type (2020-2025) & (US$ Million)
Table 26. Global RNA-Targeted Small Molecule Drugs Revenue Market Share by Type (2020-2025)
Table 27. Global RNA-Targeted Small Molecule Drugs Forecasted Market Size by Type (2026-2031) & (US$ Million)
Table 28. Global RNA-Targeted Small Molecule Drugs Revenue Market Share by Type (2026-2031)
Table 29. Global RNA-Targeted Small Molecule Drugs Market Size by Application (2020-2025) & (US$ Million)
Table 30. Global RNA-Targeted Small Molecule Drugs Revenue Market Share by Application (2020-2025)
Table 31. Global RNA-Targeted Small Molecule Drugs Forecasted Market Size by Application (2026-2031) & (US$ Million)
Table 32. Global RNA-Targeted Small Molecule Drugs Revenue Market Share by Application (2026-2031)
Table 33. North America RNA-Targeted Small Molecule Drugs Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 34. North America RNA-Targeted Small Molecule Drugs Market Size by Country (2020-2025) & (US$ Million)
Table 35. North America RNA-Targeted Small Molecule Drugs Market Size by Country (2026-2031) & (US$ Million)
Table 36. Europe RNA-Targeted Small Molecule Drugs Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 37. Europe RNA-Targeted Small Molecule Drugs Market Size by Country (2020-2025) & (US$ Million)
Table 38. Europe RNA-Targeted Small Molecule Drugs Market Size by Country (2026-2031) & (US$ Million)
Table 39. Asia-Pacific RNA-Targeted Small Molecule Drugs Market Size Growth Rate by Region (US$ Million): 2020 VS 2024 VS 2031
Table 40. Asia-Pacific RNA-Targeted Small Molecule Drugs Market Size by Region (2020-2025) & (US$ Million)
Table 41. Asia-Pacific RNA-Targeted Small Molecule Drugs Market Size by Region (2026-2031) & (US$ Million)
Table 42. Latin America RNA-Targeted Small Molecule Drugs Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 43. Latin America RNA-Targeted Small Molecule Drugs Market Size by Country (2020-2025) & (US$ Million)
Table 44. Latin America RNA-Targeted Small Molecule Drugs Market Size by Country (2026-2031) & (US$ Million)
Table 45. Middle East & Africa RNA-Targeted Small Molecule Drugs Market Size Growth Rate by Country (US$ Million): 2020 VS 2024 VS 2031
Table 46. Middle East & Africa RNA-Targeted Small Molecule Drugs Market Size by Country (2020-2025) & (US$ Million)
Table 47. Middle East & Africa RNA-Targeted Small Molecule Drugs Market Size by Country (2026-2031) & (US$ Million)
Table 48. Roche Company Details
Table 49. Roche Business Overview
Table 50. Roche RNA-Targeted Small Molecule Drugs Product
Table 51. Roche Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 52. Roche Recent Development
Table 53. Novartis Company Details
Table 54. Novartis Business Overview
Table 55. Novartis RNA-Targeted Small Molecule Drugs Product
Table 56. Novartis Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 57. Novartis Recent Development
Table 58. PTC Therapeutics Company Details
Table 59. PTC Therapeutics Business Overview
Table 60. PTC Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 61. PTC Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 62. PTC Therapeutics Recent Development
Table 63. Biogen Company Details
Table 64. Biogen Business Overview
Table 65. Biogen RNA-Targeted Small Molecule Drugs Product
Table 66. Biogen Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 67. Biogen Recent Development
Table 68. Accent Therapeutics Company Details
Table 69. Accent Therapeutics Business Overview
Table 70. Accent Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 71. Accent Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 72. Accent Therapeutics Recent Development
Table 73. Anima Biotech Company Details
Table 74. Anima Biotech Business Overview
Table 75. Anima Biotech RNA-Targeted Small Molecule Drugs Product
Table 76. Anima Biotech Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 77. Anima Biotech Recent Development
Table 78. Arrakis Pharmaceuticals Company Details
Table 79. Arrakis Pharmaceuticals Business Overview
Table 80. Arrakis Pharmaceuticals RNA-Targeted Small Molecule Drugs Product
Table 81. Arrakis Pharmaceuticals Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 82. Arrakis Pharmaceuticals Recent Development
Table 83. Epics Therapeutics Company Details
Table 84. Epics Therapeutics Business Overview
Table 85. Epics Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 86. Epics Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 87. Epics Therapeutics Recent Development
Table 88. Expansion Therapeutics Company Details
Table 89. Expansion Therapeutics Business Overview
Table 90. Expansion Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 91. Expansion Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 92. Expansion Therapeutics Recent Development
Table 93. Gotham Therapeutics Company Details
Table 94. Gotham Therapeutics Business Overview
Table 95. Gotham Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 96. Gotham Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 97. Gotham Therapeutics Recent Development
Table 98. H3 Biomedicine Company Details
Table 99. H3 Biomedicine Business Overview
Table 100. H3 Biomedicine RNA-Targeted Small Molecule Drugs Product
Table 101. H3 Biomedicine Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 102. H3 Biomedicine Recent Development
Table 103. Ribometrix Company Details
Table 104. Ribometrix Business Overview
Table 105. Ribometrix RNA-Targeted Small Molecule Drugs Product
Table 106. Ribometrix Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 107. Ribometrix Recent Development
Table 108. Skyhawk Therapeutics Company Details
Table 109. Skyhawk Therapeutics Business Overview
Table 110. Skyhawk Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 111. Skyhawk Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 112. Skyhawk Therapeutics Recent Development
Table 113. STORM Therapeutics Company Details
Table 114. STORM Therapeutics Business Overview
Table 115. STORM Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 116. STORM Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 117. STORM Therapeutics Recent Development
Table 118. Twentyeight-Seven Therapeutics Company Details
Table 119. Twentyeight-Seven Therapeutics Business Overview
Table 120. Twentyeight-Seven Therapeutics RNA-Targeted Small Molecule Drugs Product
Table 121. Twentyeight-Seven Therapeutics Revenue in RNA-Targeted Small Molecule Drugs Business (2020-2025) & (US$ Million)
Table 122. Twentyeight-Seven Therapeutics Recent Development
Table 123. Research Programs/Design for This Report
Table 124. Key Data Information from Secondary Sources
Table 125. Key Data Information from Primary Sources
Table 126. Authors List of This Report
List of Figures
Figure 1. RNA-Targeted Small Molecule Drugs Picture
Figure 2. Global RNA-Targeted Small Molecule Drugs Market Size Comparison by Type (2020-2031) & (US$ Million)
Figure 3. Global RNA-Targeted Small Molecule Drugs Market Share by Type: 2024 VS 2031
Figure 4. mRNA Translation Regulation Features
Figure 5. RNA Splicing Modification Features
Figure 6. Direct RNA Targeting Features
Figure 7. Indirect RNA Targeting - Epitranscriptomics Features
Figure 8. Global RNA-Targeted Small Molecule Drugs Market Size by Application (2020-2031) & (US$ Million)
Figure 9. Global RNA-Targeted Small Molecule Drugs Market Share by Application: 2024 VS 2031
Figure 10. SMA Case Studies
Figure 11. Oncology Case Studies
Figure 12. Lung Fibrosis Case Studies
Figure 13. Huntington's Disease Case Studies
Figure 14. Others Case Studies
Figure 15. RNA-Targeted Small Molecule Drugs Report Years Considered
Figure 16. Global RNA-Targeted Small Molecule Drugs Market Size (US$ Million), Year-over-Year: 2020-2031
Figure 17. Global RNA-Targeted Small Molecule Drugs Market Size, (US$ Million), 2020 VS 2024 VS 2031
Figure 18. Global RNA-Targeted Small Molecule Drugs Market Share by Region: 2024 VS 2031
Figure 19. Global RNA-Targeted Small Molecule Drugs Market Share by Players in 2024
Figure 20. Global Top RNA-Targeted Small Molecule Drugs Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in RNA-Targeted Small Molecule Drugs as of 2024)
Figure 21. The Top 10 and 5 Players Market Share by RNA-Targeted Small Molecule Drugs Revenue in 2024
Figure 22. North America RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 23. North America RNA-Targeted Small Molecule Drugs Market Share by Country (2020-2031)
Figure 24. United States RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 25. Canada RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 26. Europe RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 27. Europe RNA-Targeted Small Molecule Drugs Market Share by Country (2020-2031)
Figure 28. Germany RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 29. France RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 30. U.K. RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 31. Italy RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 32. Russia RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 33. Nordic Countries RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 34. Asia-Pacific RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 35. Asia-Pacific RNA-Targeted Small Molecule Drugs Market Share by Region (2020-2031)
Figure 36. China RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 37. Japan RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 38. South Korea RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 39. Southeast Asia RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 40. India RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 41. Australia RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 42. Latin America RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 43. Latin America RNA-Targeted Small Molecule Drugs Market Share by Country (2020-2031)
Figure 44. Mexico RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 45. Brazil RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 46. Middle East & Africa RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 47. Middle East & Africa RNA-Targeted Small Molecule Drugs Market Share by Country (2020-2031)
Figure 48. Turkey RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 49. Saudi Arabia RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 50. UAE RNA-Targeted Small Molecule Drugs Market Size YoY Growth (2020-2031) & (US$ Million)
Figure 51. Roche Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 52. Novartis Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 53. PTC Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 54. Biogen Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 55. Accent Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 56. Anima Biotech Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 57. Arrakis Pharmaceuticals Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 58. Epics Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 59. Expansion Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 60. Gotham Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 61. H3 Biomedicine Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 62. Ribometrix Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 63. Skyhawk Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 64. STORM Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 65. Twentyeight-Seven Therapeutics Revenue Growth Rate in RNA-Targeted Small Molecule Drugs Business (2020-2025)
Figure 66. Bottom-up and Top-down Approaches for This Report
Figure 67. Data Triangulation
Figure 68. Key Executives Interviewed